Op-brai160064 1723..1734

نویسندگان

  • Paola S. Denora
  • Katrien Smets
  • Federica Zolfanelli
  • Chantal Ceuterick-de Groote
  • Carlo Casali
  • Tine Deconinck
  • Anne Sieben
  • Michael Gonzales
  • Stephan Zuchner
  • Frédéric Darios
  • Dirk Peeters
  • Alexis Brice
  • Alessandro Malandrini
  • Peter De Jonghe
  • Filippo M. Santorelli
  • Giovanni Stevanin
  • Jean-Jacques Martin
  • Khalid H. El Hachimi
چکیده

The most common form of autosomal recessive hereditary spastic paraplegia is caused by mutations in the SPG11/KIAA1840 gene on chromosome 15q. The nature of the vast majority of SPG11 mutations found to date suggests a loss-of-function mechanism of the encoded protein, spatacsin. The SPG11 phenotype is, in most cases, characterized by a progressive spasticity with neuropathy, cognitive impairment and a thin corpus callosum on brain MRI. Full neuropathological characterization has not been reported to date despite the description of4100 SPG11 mutations. We describe here the clinical and pathological features observed in two unrelated females, members of genetically ascertained SPG11 families originating from Belgium and Italy, respectively. We confirm the presence of lesions of motor tracts in medulla oblongata and spinal cord associated with other lesions of the central nervous system. Interestingly, we report for the first time pathological hallmarks of SPG11 in neurons that include intracytoplasmic granular lysosome-like structures mainly in supratentorial areas, and others in subtentorial areas that are partially reminiscent of those observed in amyotrophic lateral sclerosis, such as ubiquitin and p62 aggregates, except that they are never labelled with anti-TDP-43 or anti-cystatin C. The neuropathological overlap with amyotrophic lateral sclerosis, associated with some shared clinical manifestations, opens up new fields of investigation in the physiopathological continuum of motor neuron degeneration.

برای دانلود رایگان متن کامل این مقاله و بیش از 32 میلیون مقاله دیگر ابتدا ثبت نام کنید

ثبت نام

اگر عضو سایت هستید لطفا وارد حساب کاربری خود شوید

منابع مشابه

Solvation Parameters of Solutes: An Attempt of Improvements in Characterization and Determination

We are presenting here an updated version of our predictive model of solvation parameters of solutes, based on a simplified molecular topology (J. Chem. Inf. Model, 2006, 46, 1723-1734). The learning experimental database of this model is presently larger than in our first version and includes more compounds with more than one functional group of the same type. This experimental database is als...

متن کامل

Laparoscopic Excision Versus Open Excision for the Treatment of Choledochal Cysts: A Systematic Review and Meta-Analysis

In 1723, Vater first described choledochal cyst and in 1977, Todani et al classified this disease. For many years, open excision (OP) as the standard procedure made a great impact in the treatment of choledochal cyst. Since 1995, when Farello et al first reported laparoscopic choledochal cyst excision, laparoscopic excision (LA) has been used worldwide. However, its safety remains a major conce...

متن کامل

Monitoring and Managing the Harvest of Tegu Lizards in Paraguay

Despite the ongoing worldwide trade in reptiles, monitoring and management systems are only recently being developed for exploited lizards and snakes. We studied the tegu lizard (Tupinambis spp.) management and harvest monitoring program in Paraguay as a model for commercially exploited reptile management. Tegu lizards are among the most exploited reptiles in the world, with current quotas for ...

متن کامل

On synchronal algorithm for fixed point and variational inequality problems in hilbert spaces

The aim of this article is to expand and generalize some approximation methods proposed by Tian and Di (J Fixed Point Appl, 2011. doi:10.1186/1687-1812-21) to the class of [Formula: see text]-total asymptotically strict pseudocontraction to solve the fixed point problem as well as variational inequality problem in the frame work of Hilbert space. Further, the results presented in this paper ext...

متن کامل

ذخیره در منابع من


  با ذخیره ی این منبع در منابع من، دسترسی به آن را برای استفاده های بعدی آسان تر کنید

عنوان ژورنال:

دوره   شماره 

صفحات  -

تاریخ انتشار 2016